New Gene Therapy Success In A Rare Disease Of The Immune System | Eurekalert! Science News | Caramengh2c

This Cara Meningkatkan Trombosit study, which is ongoing, assesses the feasibility and efficacy of gene therapy in this indication. The article published in JAMA reports the results for the first six patients, aged 8 months to 16 years, where the monitoring period allowed assessment of the initial effects of the treatment.
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